MyoAAV for Targeted Skeletal Muscle Delivery for DMD & XLMTM

Time: 1:00 pm
day: Post-Conference Day


  • A family of muscle-tropic capsids identified by directed evolution in mice and primates
  • MyoAAV transduction is dependent on integrin heterodimers in mouse and human cells
  • MyoAAV administration at low dose results in therapeutic efficacy in disease models
  • Systemically-administered MyoAAV transduces primate muscles highly efficiently