Optimizing Long Term Follow Up Strategies & Data Collection for Future Muscular Disorder Studies

Time: 9:10 am
day: Day Two


  • The requirements for long-term follow up of gene therapy trial participants and for those who receive an approved gene therapy add complication and cost to the development of these therapies
  • The Muscular Dystrophy Association’s Care Center Network and MOVR database are being positioned to help meet the needs for administration and long-term follow-up of gene therapy recipients