Perry Shieh

Company: Astellas Gene Therapies

Job title: Professor of Neurology & Pediatrics, University of California Los Angeles & Principal Investigator for ASPIRO

Seminars:

Panel Discussion: The Race for A Cure: Field Update of Muscular Disorders Gene Therapy Programs 9:15 am

Addressing older patient populations & introducing even larger doses Clinicians managing the adverse effects: myocarditis and liver toxicity Discussing predisposition to adverse side effectsRead more

day: Day One

A Clinician’s Perspective: Gene Therapy for X-Linked Myotubular Myopathy 8:45 am

-X-Linked Myotubular Myopathy (XLMTM): Burden of disease Gene therapy and efficacy outcomes Safety profile and liver toxicityRead more

day: Day One