Expert Speaker Faculty

Catja Freiburghaus

Senior Scientist, Clinical Development Lead Gene Therapy

Hansa Biopharma

Chris Rusconi

Chief Development Officer

DiNAQOR

Dawn Phillips

Senior Director - Clinical Outcomes Research

REGENXBIO

Greg Luerman

Vice President, Research & Partnerships

Curi Bio

HEATHER FITZPATRICK MEDLIN

Sr, Director

CureDuchenne

James Warren

Senior Vice President - Pharmaceutical Development

Ultragenyx

Kathy Ivey

Vice President - Gene Therapy & Research

Tenaya Therapeutics

Kristin Stephenson

Director - Office of Strategy & Alliances, Pediatric Translational Neuroscience Initiative

St. Jude Children's Research Hospital

Lena Winstedt

Global Franchise Lead Gene Therapy

Hansa Biopharma

Lianna Orlando

Vice President - Research & Partner

CureDuchenne

Mindy Cameron

Life Sciences Consultant

AdvocacyWorks

Mitra Tavakkoli

Former Vice President, Clinical Development

4D Molecular Therapeutics

Morten Sogaard

President and Division Head, Gene Therapy Research & Technical Operations

Astellas Gene Therapies

Naresh Kumar Meena

Researcher

NIH

Richard Parad

Director - New-born Genomic Medicine Program - Department of Paediatrics

Brigham Women's Hospital

Sharif Tabebordbar

Chief Scientific Officer

Kate Therapeutics

Sharon McGonigle

Vice President, Research &Development

Solid Biosciences

Sonia Albini

Principal scientist

Genethon

Yu (Eric) Zheng

Principal Scientist – Neuromuscular Gene Editing

PRIME Medicine