Assessing the Durability of Gene Therapies for Muscular Disorders and Discussing the Potential for Redosing

Time: 9:00 am
day: Pre-Conference Day


As research progresses, advancements in vector technology, optimization of gene delivery strategies and immune supression techniques are expected to further enhance the durability of gene therapies, paving the way for a new era in the treatment of debilitating muscular conditions. Join this workshop to discuss recent advancements and the potential for readministration strategies for muscular gene therapies.

Attend this workshop to learn about:

  • Current techniques for assessing durability and efficacy in slow progressing diseases
  • Examining dosing strategies to get the best outcome in growing muscle cells
  • Navigating the challenges of developing a therapy where the durability is unknown
  • Deep dive into current potential redosing strategies
  • Discussing the potential for immunomodulators to facilitate redosing gene therapies to the muscles