Supporting Patients and Caregivers Through the Changing Epidemiology of Degenerative Muscular Diseases and Long-term Trial Follow Up

Time: 2:30 pm
day: Day One


  • Harnessing epidemiological studies to better predict the impact of treatment and manage expectations
  • Discussing systematic approaches to collecting data before and during longterm trials that is manageable for patients and caregivers
  • Longitudinal monitoring techniques