Jamie Marshall

Company: Solid Biosciences

Job title: Principal Scientist

Seminars:

Non-Clinical Studies Using a Novel Muscle-Targeted Capsid 10:45 am

Delivering microdystrophin via a novel, muscle targeting capsid Clearing IND for the treatment of DMD Harnessing preclinical studies to smoothly translate into first-in-human studiesRead more

day: Day Two

Panel Discussion – Improving Delivery to the Muscle Cells to Reduce the Necessary Dosage 11:45 am

The current state of play of vectors being used for muscular delivery Reducing the CG content of vectors to reduce immune response and increase transgene expression Discussing optimal promotors to improve AAV muscle targeting and reduce dosageRead more

day: Day Two